Gene Therapy May Help Address Remaining Unmet Needs in Hypertrophic Cardiomyopathy
November 13th 2023Milind Desai, MD, MBA, an investigator on the MyPeak-1 trial and the director of the Hypertrophic Cardiomyopathy Center and the vice chair of the Heart Vascular Thoracic Institute at the Cleveland Clinic, discussed Tenaya Therapeutics’ TN-201.
Setting the Stage for Engineered B-Cell Therapies in Cancer and Autoimmune Disease
November 7th 2023David Rawlings, MD, the director of the Center for Immunity and Immunotherapies at Seattle Children's Research Institute, discussed findings from several preclinical studies that could help push engineered B-cell therapies towards clinical trials.
University of Manchester Launches MPS II Gene Therapy Trial, Picking Up Where AVROBIO Left Off
November 5th 2023UoM was previously collaborating on the development of AVR-RD-05 with AVROBIO, but regained the license to the HSC gene therapy following the company’s cessation of development on all programs.