Lysosomal Disorders

The CGTLive Lysosomal Disorders specialty topic page contains video interviews with key opinion leaders discussing the most relevant FDA actions, clinical guideline updates, and clinical trial findings related to cell therapies, gene therapies, and engineered and regenerative medicines developed for Lysosomal storage diseases. It also houses the most up-to-date clinical news coverage in the field of gene and cell therapy for diseases related to lysosomal storage and dysfunction.

Latest News

Around the Helix: Cell and Gene Therapy Company Updates – November 20, 2024
Around the Helix: Cell and Gene Therapy Company Updates – November 20, 2024

November 20th 2024

Catch up on the latest news, breakthroughs, and announcements from biotechnology companies making advancements in cell and gene therapies.

CGTLive®’s Weekly Rewind
CGTLive®’s Weekly Rewind – November 15, 2024

November 15th 2024

FDA Approves PTC Therapeutics’ Gene Therapy Kebilidi for AADC Deficiency
FDA Approves PTC Therapeutics’ Gene Therapy Kebilidi for AADC Deficiency

November 13th 2024

Around the Helix: Cell and Gene Therapy Company Updates – November 13, 2024
Around the Helix: Cell and Gene Therapy Company Updates – November 13, 2024

November 13th 2024

CGTLive®’s Weekly Rewind
CGTLive®’s Weekly Rewind – November 8, 2024

November 8th 2024

Video Interviews
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