Lysosomal Disorders

The CGTLive Lysosomal Disorders specialty topic page contains video interviews with key opinion leaders discussing the most relevant FDA actions, clinical guideline updates, and clinical trial findings related to cell therapies, gene therapies, and engineered and regenerative medicines developed for Lysosomal storage diseases. It also houses the most up-to-date clinical news coverage in the field of gene and cell therapy for diseases related to lysosomal storage and dysfunction.

Latest News

CGTLive®’s Weekly Rewind
CGTLive®’s Weekly Rewind – January 17, 2025

January 17th 2025

Review top news and interview highlights from the week ending January 17, 2025.

Around the Helix: Cell and Gene Therapy Company Updates – January 15, 2025
Around the Helix: Cell and Gene Therapy Company Updates – January 15, 2025

January 15th 2025

CGTLive®’s Weekly Rewind
CGTLive®’s Weekly Rewind – January 10, 2025

January 10th 2025

Around the Helix: Cell and Gene Therapy Company Updates – January 8, 2025
Around the Helix: Cell and Gene Therapy Company Updates – January 8, 2025

January 8th 2025

Heather Lau, MD, MS
Ultragenyx Puts BLA for MPSIII Gene Therapy UX111 in Front of FDA

January 7th 2025

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Podcasts
ImmunoLogic
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