Published: August 16th 2024 | Updated: August 19th 2024
Uptake of Nononcology Gene Therapy Remains Slow in Hematology
Published: March 18th 2024 | Updated: June 3rd 2024
Phase 3 Trial Seeks to Continue Supporting Arsa-Cel Gene Therapy for MLD
Published: May 12th 2025 | Updated: May 17th 2025
Aneal Khan, MD, MSc, FCCMG, FRCPC, on Evaluating Gene Therapy for Fabry Disease
Published: May 15th 2025 | Updated: May 17th 2025
Rebecca Ahrens-Nicklas, MD, PhD; and Kiran Musunuru, MD, PhD, MPH, ML, MRA, on Treating CPS1 Deficiency With Personalized Gene Editing
Published: May 13th 2025 | Updated: May 17th 2025
Spur Therapeutics’ Gene Therapy SBT101 Generally Well Tolerated in Phase 1 Trial for Adrenoleukodystrophy
Published: September 27th 2023 | Updated: May 17th 2025
FDA AdComm Votes Down BrainStorm Cell Therapeutics’ ALS Cell Therapy NurOwn