PJ Brooks, PhD, on Developing New Strategies for Novel Clinical Trials
The deputy director, Division of Rare Diseases Research Innovation, NCATS, NIH, discussed the NIH’s genome editing program and more.
PJ Brooks, PhD, on Strategies to Facilitate NMD Therapy Development
The deputy director, Division of Rare Diseases Research Innovation, NCATS, NIH, discussed initiatives including the BGTC and the platform vector gene therapy project.
PJ Brooks, PhD, on Working to Bring Gene Therapy Development to More Neuromuscular Disorders