Lysosomal Disorders

Latest News

February 4th 2026
Around the Helix: Cell and Gene Therapy Company Updates – February 4, 2026

Catch up on the latest news, breakthroughs, and announcements from biotechnology companies making advancements in cell and gene therapies.

CGTLive®’s Weekly Rewind
January 30th 2026

CGTLive®’s Weekly Rewind – January 30, 2026

January 28th 2026

Around the Helix: Cell and Gene Therapy Company Updates – January 28, 2026

CGTLive®’s Weekly Rewind
January 23rd 2026

CGTLive®’s Weekly Rewind – January 23, 2026

January 21st 2026

Around the Helix: Cell and Gene Therapy Company Updates – January 21, 2026

Latest Videos

Podcasts

ImmunoLogic Bonus Episode
ImmunoLogic, Bonus Episode: "Chemo Optional, Data Mandatory - A Year-End Recap"
ImmunoLogic Bonus Episode
ImmunoLogic, Bonus Episode: "ASH 2025: Practice-Changers on the Ground and on the Wi‑Fi"
ImmunoLogic Episode 7
ImmunoLogic, Episode 7: "Turbocharging CAR T-Cells: The IL-9 Orthogonal Signal" With Anusha Kalbasi, MD
Special Report Episode 10
Quarter Century Update: The Impact of Artificial Intelligence
Special Report Episode 9
Quarter Century Update: Thoughts on Reducing Costs of Goods
Special Report Episode 7
Quarter Century Update: Future Predictions for the Field
Special Report Episode 7
Quarter Century Update: What Does the Field Need Most Right Now?
Special Report Episode 6
Quarter Century Update: What Lessons Should Guide the Next Generation of Developers and Regulators?
Special Report Episode 5
Quarter Century Update: The Continued Unknowns of Cell and Gene Therapy
Special Report Episode 4
Quarter Century Update: How can Partnerships Between Academia, Biotech, and Pharma be Better Structured?

CME Content

View More
Show Me the Data: How Today’s Evidence Is Shaping Tomorrow’s Management and Prophylaxis of Chronic GVHD
In-Person Event

Show Me the Data: How Today’s Evidence Is Shaping Tomorrow’s Management and Prophylaxis of Chronic GVHD

February 7, 2026

Register now!
Medical Crossfire®: Menin Inhibitors in AML—Dissecting the Data to Define the Role
Virtual Event

Medical Crossfire®: Menin Inhibitors in AML—Dissecting the Data to Define the Role

February 17, 2026

View more
30th Annual International Congress on Hematologic Malignancies®: Focus on Leukemias, Lymphomas, and Myeloma
In-Person Event

30th Annual International Congress on Hematologic Malignancies®: Focus on Leukemias, Lymphomas, and Myeloma

February 26-28, 2026

Register now!
Medical Crossfire®: Expert Interpretations of the Latest Data in CLL Management – Understanding the Impact of Optimal Treatment Selection on Patient Outcomes
Video

Medical Crossfire®: Expert Interpretations of the Latest Data in CLL Management – Understanding the Impact of Optimal Treatment Selection on Patient Outcomes

Jennifer R. Brown, MD, PhD; Alexey V. Danilov, MD, PhD; Matthew S. Davids, MD, MMSc

View more
Community Practice Connections™: Tailored Treatment Approaches for Older Patients With Advanced HR+/HER2– Breast Cancer
Multimedia

Community Practice Connections™: Tailored Treatment Approaches for Older Patients With Advanced HR+/HER2– Breast Cancer

Hope S. Rugo, MD, FASCO; Neil M. Iyengar, MD; Komal Jhaveri, MD, FACP

View more
29th Annual International Congress on Hematologic Malignancies: Focus on Leukemias, Lymphomas, and Myeloma
Video

29th Annual International Congress on Hematologic Malignancies: Focus on Leukemias, Lymphomas, and Myeloma

André H. Goy, MD; Jorge E. Cortes, MD; Sagar Lonial, MD, FACP

View more
Medical Crossfire®: Harnessing the Power of Modern Therapies in Newly Diagnosed Multiple Myeloma
Video

Medical Crossfire®: Harnessing the Power of Modern Therapies in Newly Diagnosed Multiple Myeloma

C. Ola Landgren, MD, PhD; Mohamad Mohty, MD, PhD; Surbhi Sidana, MD

View more
Cases & Conversations™: Transforming AML Care—Precision Strategies, Evolving Therapies, and Clinical Insights
Video

Cases & Conversations™: Transforming AML Care—Precision Strategies, Evolving Therapies, and Clinical Insights

Gail J. Roboz, MD; Hagop Kantarjian, MD; Catherine Lai, MD, MPH; Amer Zeidan, MBBS, MHS

View more
Cases and Conversations™: Sorting Through the Expanding Treatment Options for Patients with Relapsed/Refractory Multiple Myeloma
Video

Cases and Conversations™: Sorting Through the Expanding Treatment Options for Patients with Relapsed/Refractory Multiple Myeloma

C. Ola Landgren, MD, PhD; Mohamad Mohty, MD, PhD; Surbhi Sidana, MD

View more
Medical Crossfire®: Improving Patient Outcomes in Myeloproliferative Neoplasms With Novel Therapeutic Approaches
Video

Medical Crossfire®: Improving Patient Outcomes in Myeloproliferative Neoplasms With Novel Therapeutic Approaches

Rami Komrokji, MD; Gabriela Hobbs, MD; John Mascarenhas, MD; Naveen Pemmaraju, MD

View more
Expert Perspectives on Applying Recent Evidence to Practice in the Management of Newly Diagnosed Multiple Myeloma
Video

Expert Perspectives on Applying Recent Evidence to Practice in the Management of Newly Diagnosed Multiple Myeloma

Amrita Krishnan, MD; Meletios Athanasios (Thanos) C. Dimopoulos, MD; Shaji Kumar, MD; Katja Weisel, MD

View more

More News