Any T-cell-mediated disease benefits from therapy without affecting other inflammatory pathways
CGTLive®’s Weekly Rewind – January 10, 2025
Review top news and interview highlights from the week ending January 10, 2025.
CGTLive® Presents: ImmunoLogic, A Video Podcast With Joseph Fraietta, PhD
Hosted by Joseph Fraietta, PhD, ImmunoLogic will be tailored for an audience fluent in the language of medicine and biotechnology, offering data-driven insights while maintaining accessibility.
Tenaya’s Hypertrophic Cardiomyopathy Gene Therapy TN-201 Well-Tolerated in Early Clinical Data
The data comes from 3 patients treated at the trial’s low dose.
The Promise of Cell Therapy Approaches in Epilepsy
Mind Moments®, a podcast from our sister site NeurologyLive®, held an exclusive interview with Jonathan Parker, MD, PhD.
RESTEM’s ULSC Therapy Restem-L Fast Tracked by FDA for Idiopathic Inflammatory Myopathy
Restem-L previously received orphan drug designation from the FDA for PM/DM in December 2024.
Ultragenyx Puts BLA for MPSIII Gene Therapy UX111 in Front of FDA
Ultragenyx is seeking accelerated approval for the BLA based on the use of CSF heparan sulfate data from the phase 1/2/3 Transpher A clinical trial.