Gainesville, FL-Scientists seeking to use gene therapy to reverse a form of inherited blindness have won a $9.8-million grant from the National Institutes of Health (NIH).
First Patient With Multiple Myeloma Dosed in EsoBiotec's Trial for In Vivo CAR-T ESO-T01
According to EsoBiotec, this is the first time a patient has been treated with an in vivo BCMA-directed CAR-T therapy in a clinical trial.
CGTLive® Presents: ImmunoLogic, A Video Podcast With Joseph Fraietta, PhD
Hosted by Joseph Fraietta, PhD, ImmunoLogic will be tailored for an audience fluent in the language of medicine and biotechnology, offering data-driven insights while maintaining accessibility.
Around the Helix: Cell and Gene Therapy Company Updates – January 8, 2025
Catch up on the latest news, breakthroughs, and announcements from biotechnology companies making advancements in cell and gene therapies.
The Promise of Cell Therapy Approaches in Epilepsy
Mind Moments®, a podcast from our sister site NeurologyLive®, held an exclusive interview with Jonathan Parker, MD, PhD.
Ultragenyx Puts BLA for MPSIII Gene Therapy UX111 in Front of FDA
Ultragenyx is seeking accelerated approval for the BLA based on the use of CSF heparan sulfate data from the phase 1/2/3 Transpher A clinical trial.
Arbor Biotechnologies’ CRISPR-Based Gene Editing Therapy ABO-101 Cleared for US Trial in Primary Hyperoxaluria Type 1
Arbor noted it has designed redePHine, a phase 1/2 clinical trial (NCT identifier pending) that will evaluate ABO-101 in adults and children with PH1.