CGTLive’s Weekly Rewind – September 23, 2022
Review top news and interview highlights from the week ending September 23, 2022.
Welcome to CGTLive’s Weekly Rewind! We’ve compiled 5 highlights from this week’s coverage of advances in gene and cell therapies, including FDA actions, notable research, and interviews with experts across the field.
1. Eli-Cel Approved for CALD, Marking Second Gene Therapy Win for bluebird bio
The approval follows unanimous support of eli-cel's benefits in CALD from an FDA AdComm meeting and an approval for beti-cel in beta-thalassemia.
2. Roberto Giugliani, MD, PhD, on Reducing GAGs in MPS Type 2 With Gene Therapy
The professor of genetics at Federal University of Rio Grande do Sul discussed updated data from the CAMPSIITE trial.
3. Zevor-Cel Yields 100% ORR in R/R Multiple Myeloma
Eleven patients in the LUMMICAR-2 trial were evaluable for preliminary efficacy analyses.
4. David S. Hong, MD, on the SURPASS Clinical Trial and TCR T-cell Therapy in Solid Tumors
Hong presented data from the SURPASS clinical trial at the 2022 European Society for Medical Oncology (ESMO) Congress.
5. Intellia Nets Positive Data Across In Vivo CRISPR Therapies for ATTR Amyloidosis Cardiomyopathy, Angioedema
Administration of NTLA-2001 led to rapid and deep reductions in serum TTR by day 28.
Evaluating Allogeneic CAR-T P-BCMA-ALLO1 in R/R Multiple Myeloma
November 21st 2024Bhagirathbhai R. Dholaria, MD, an associate professor of medicine in malignant hematology & stem cell transplantation at Vanderbilt University Medical Center, discussed interim data from the phase 1/1b clinical trial evaluating Poseida's CAR-T.
World Pancreatic Cancer Day 2024: Looking Back at Progress in Cell and Gene Therapy
November 21st 2024In observance of World Pancreatic Cancer Day, held on the third Thursday of November each year, we took a look back at the past year's news in cell and gene therapy for pancreatic cancer indications.
