CGTLive’s Weekly Rewind – July 29, 2022

Article

Review top news and interview highlights from the week ending July 29, 2022.

Welcome to CGTLive’s Weekly Rewind! We’ve compiled 5 highlights from this week’s coverage of advances in gene and cell therapies, including FDA actions, notable research, and interviews with experts across the field.

1. Editas' Gene Therapy Trial for Sickle Cell Initiates After Hold Lifted

The company announced successful neutrophil and platelet engraftment for the first patient dosed.

2. Nilanjan Ghosh, MD, PhD, on New Avenues of CAR T Research in Lymphoma

The chief of the lymphoma division and oncologist at Levine Cancer Institute discussed new CAR T-cell therapies being investigated for hematologic malignancies.

3. Gamma-Delta T-cell Therapy Shows Durable Complete Responses in Acute Myeloid Leukemia

All 3 patients remained progression-free at more than 1 year post-treatment.

4. Susan Ruediger on Partnering to Develop CMT Gene Therapies

Susan Ruediger, founder and chief mission officer, CMT Research Foundation, discussed a new partnership with Nationwide Children’s Hospital.

5. Nanoscope Gene Therapy Continues Progress in Stargardt Disease

Data is expected in the first quarter of 2023 for both Stargardt disease and retinitis pigmentosa.

Recent Videos
Barry J Byrne, MD, PhD, the chief medical advisor of MDA and a physician-scientist at the University of Florida
Sarah Larson, MD, the medical director of the Immune Effector Cell Therapy Program in the Division of Hematology/Oncology at David Geffen School of Medicine at University of California, Los Angeles (UCLA)
Manali Kamdar, MD, the associate professor of medicine–hematology and clinical director of lymphoma services at the University of Colorado
Manali Kamdar, MD, the associate professor of medicine–hematology and clinical director of lymphoma services at the University of Colorado
Ben Samelson-Jones, MD, PhD, assistant professor pediatric hematology, Perelman School of Medicine, University of Pennsylvania and Associate Director, Clinical In Vivo Gene Therapy, Children’s Hospital of Philadelphia
Manali Kamdar, MD, the associate professor of medicine–hematology and clinical director of lymphoma services at the University of Colorado
Steven W. Pipe, MD, a professor of pediatric hematology/oncology at CS Mott Children’s Hospital
Haydar Frangoul, MD, the medical director of pediatric hematology/oncology at Sarah Cannon Research Institute and Pediatric Transplant and Cellular Therapy Program at TriStar Centennial
Bhagirathbhai R. Dholaria, MD, an associate professor of medicine in malignant hematology & stem cell transplantation at Vanderbilt University Medical Center
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