Review top news and interview highlights from the week ending April 4, 2025.
CGTLive®’s Weekly Rewind
Welcome to CGTLive®’s Weekly Rewind! We’ve compiled 5 highlights from this week’s coverage of advances in gene and cell therapies, including FDA actions, notable research, and interviews with experts across the field.
The product is marketed under the name Qfitlia.
The chief executive officer of Eledon Pharmaceuticals also discussed other future plans for the company.
The move was made in relation to the previously-announced death of a US teenager who received the therapy.
Robert Califf, MD, MACC, a cardiologist and former FDA commissioner, discussed the necessity of policy and funding efforts for neuromuscular disorders, the stress on the clinical care system, and the need to acknowledge healthcare inequities.
At 12 weeks posttreatment, all 4 of the patients showed improvement in the form of a lower logMAR.
Urgency of Funding and Equity in Neuromuscular Research and Care
March 31st 2025Robert Califf, MD, MACC, a cardiologist and former FDA commissioner, discussed the necessity of policy and funding efforts for neuromuscular disorders, the stress on the clinical care system, and the need to acknowledge healthcare inequities.