Breakthrough seen in canine Leber's congenital amaurosis

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Philadelphia-Gene therapy has successfully restored the visual function of blind dogs with a rare congenital retinal disease, according to early research results. This breakthrough holds implications for the treat- ment of several human retinal degenerative diseases within the next several years.

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David Barrett, JD, the chief executive officer of ASGCT
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David Barrett, JD, the chief executive officer of ASGCT
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Nirav Shah, MD, MSHP, associate professor of medicine, at the Medical College of Wisconsin
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